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ACCUEIL - Association Française de CRIGLER-NAJJAR

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ACCUEIL - Association Française de CRIGLER-NAJJAR | crigler-najjar.fr Reviews
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Présentation du site de l'Association Française de CRIGLER-NAJJAR
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1 philippe labrune
2 nicolas ferry
3 bilirubine
4 ictere
5 jaunisse
6 de gilbert
7 hepatite
8 neurotoxicite
9 appareil phototherapie
10 lumiere bleue
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ACCUEIL - Association Française de CRIGLER-NAJJAR | crigler-najjar.fr Reviews

https://crigler-najjar.fr

Présentation du site de l'Association Française de CRIGLER-NAJJAR

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1

Année 2012 - Association Française de CRIGLER-NAJJAR

http://www.crigler-najjar.fr/annee-2012

En route pour des essais de thérapie génique menés par Généthon! Poursuite de la mise au point des vecteurs dans le but de réaliser des essais cliniques sur des patients Crigler-Najjar. Ce programme est mené en partenariat avec Généthon. Qui produira les lots précliniques, ainsi que les lots cliniques du vecteur médicament AAV-UGT1A1 qui seront administrés chez les patients. Les études précliniques actuellement en cours serviront de base à la mise en place d’un essai clinique de Phase I/II. Démarrage d&#...

2

9 avril 2015 - Association Française de CRIGLER-NAJJAR

http://www.crigler-najjar.fr/9-avril-2015

L’AFM-Téléthon annonce les futurs essais de thérapie génique sur la maladie de Crigler-Najjar dans son communiqué de presse du 9 avril 2015. Lire le communiqué de presse. À l’attention des médecins, urgentistes et patients). Convertisseur de taux de bilirubine. Août 2016 >. Partenaire de notre association. Mise à jour: lundi 22 août 2016. Association Française de CRIGLER-NAJJAR.

3

7 mai 2015 - En route vers des essais cliniques - Association Française de CRIGLER-NAJJAR

http://www.crigler-najjar.fr/7-mai-2015-en-route-vers-des

7 mai 2015 - En route vers des essais cliniques. 7 mai 2015 - En route vers des essais cliniques. Une nouvelle avancée dans la thérapie génique : le syndrome de Crigler-Najjar. Federico Mingozzi, responsable de l’équipe Immunologie et Thérapie Génique dans les maladies du foie à Généthon, a présenté des travaux qui prouvent sur les rongeurs l’efficacité d’une thérapie génique dans une maladie rare du foie, le syndrome de Crigler-Najjar. Une seule injection nécessaire. Vers un essai clinique de phase I/II.

4

Année 2005 - Association Française de CRIGLER-NAJJAR

http://www.crigler-najjar.fr/annee-2005

En route pour des essais de thérapie génique menés par Généthon! Chercheur en thérapie génique, du CHU de Nantes, travaille sur notre maladie depuis de nombreuses années déjà. Nicolas Ferry représente pour tous nos malades , un grand espoir. En effet, celui-ci vient tout récemment, de réussir à guérir complètement des rats Gunn atteints de la maladie de Crigler-Najjar. Il vient de publier en août 2005, dans la revue Hépathologie, le résultat de ses travaux ( Successful Gene Therapy of the Gunn Rat. Des e...

5

Photothérapie - Association Française de CRIGLER-NAJJAR

http://www.crigler-najjar.fr/phototherapie

En route pour des essais de thérapie génique menés par Généthon! Est un traitement utilisant de gros appareils diffusant une lumière bleue. Pour dégrader la bilirubine. Qui se trouve à la surface de la peau uniquement (on ne traite pas en profondeur). On n’élimine ainsi qu’une toute petite partie de la bilirubine. Mais la bilirubine étant produite en continu, il faut donc traiter en permanence ; La durée et la surface d’exposition sont très importantes. Les parents doivent donc se débrouiller seuls pour ...

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bililed.com bililed.com

Links

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Phototherapy lamp for the Crigler-Najjar Syndrome. Stichting Najjar Gilze Rijen. Crigler Najjar Syndrome (USA). Association Française de Crigler-Najjar. Asociacion Espanola de Sindrome de Crigler-Najjar. Daytime Phototherapy for Crigler Najjar Syndrome (USA). The Journal of Norwegian Medical Association.

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Friends Association

http://www.itcotation.com/friends

Friends association, moselle, france, maladie, enfant, rare, dons, partenaires, football, maillot, crigler,najjar, elena, sarreguemines, forbach, metz, freyming, cocheren, football, 2014,. Ils nous soutiennent . Organise des événements pour venir. En Aide à des bonnes causes. A été créée le 8 février 2011. Depuis cette date, notre activité principale est dorganiser des événements pour apporter notre soutien aux associations dans le besoin . Dire dexposition à une lumière bleue spéciale (environ 12h/24h).

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ACCUEIL - Association Française de CRIGLER-NAJJAR

Association Française de CRIGLER-NAJJAR. Généthon démarre les essais de thérapie génique sur la maladie de Crigler-Najjar. Une maladie plus qu’orpheline. Lire la suite .). Malgré l’extrême rareté de cette maladie, la recherche avance à grands pas et des essais cliniques sur des malades, financés grâce au TELETHON, devraient débuter bientôt. Voir les vidéos en page recherche. En attendant les progrès de la recherche, pour ces enfants, la photothérapie. 10 à 12 heures sur 24! Lire la suite .). Généthon, le...

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